Gene therapies offer a completely new way of treating a range of serious diseases. But before we can realize their full potential, a...

This Sunday, February 28th marks the 14th Rare Disease Day. Patients, advocates, providers, and others around the world recognize this...

WASHINGTON, DC (December 23, 2020) – Today, the Institute for Gene Therapies (IGT) Chairman Congressman Erik Paulsen issued the following...

CureDuchenne’s mission is to improve the lives of everyone affected by Duchenne through accelerating research to find the cure, improving...

September is Newborn Screening Awareness Month, a dedicated time to educate the public about this critical screening. IGT advocates for...

By Jennifer McNary, mother of two sons with Duchenne muscular dystrophy, patient advocate and founder of One Rare. For all the incredible...

One of our founding Patient Advisory Council Members, the EveryLife Foundation for Rare Diseases, is a 501(c)(3) nonprofit, nonpartisan...

Proposed rule advances longstanding priority for gene therapy stakeholders FOR IMMEDIATE RELEASE July 20, 2020 CONTACT: Macey Kostbar,...

On Monday, July 13, the Institute for Gene Therapies (IGT) held a conversation with recognized experts on the CMS proposed rule that...

On Monday, July 13, 2020 at 4 PM Eastern Time, the Institute for Gene Therapies (IGT) will host a conversation with recognized experts...